2021 FDA Registration Trials’ Reviews

  • PEMBROLIZUMAB for adjuvant treatment of Stage IIB or IIC melanoma (3 Dec 2021)

    REGULAR APPROVAL for “the adjuvant treatment of adult and pediatric (≥12 years of age) patients with stage IIB or IIC melanoma following complete resection.”

    Based on the KEYNOTE-716 trial

    1 - DESIGN:

    2 - EFFICACY:

    3 - TOXICITY:

    Critical appraisal:

    Overall conclusion:

  • SELPERCATINIB for lung and thyroid cancers with RET gene mutations or fusions

    ACCELERATED APPROVAL for “
    - Adult patients with metastatic RET fusion-positive non-small cell lung cancer (NSCLC);
    - Adult and pediatric patients ≥12 years of age with advanced or metastatic RET-mutant medullary thyroid cancer (MTC) who require systemic therapy;
    - Adult and pediatric patients ≥12 years of age with advanced or metastatic RET fusion-positive thyroid cancer who require systemic therapy and who are radioactive iodine-refractory (if radioactive iodine is appropriate).”

    Based on the LIBRETTO-001 trial:
    - NSCLC
    - thyroid